8 min read | February 2026 HD research recap: published trial data from branaplam trial; new insights into the genetics of the HD “grey zone”; plus worms, brain circuits, eye tracking, and the hidden ...
In a groundbreaking first, a gene therapy in clinical trials has slowed the progression of Huntington's disease, a rare genetic disorder in which toxic bits of protein cause brain cells to malfunction ...
ST. LOUIS — Scientists may have reached a breakthrough in the fight against Huntington’s disease, a rare and fatal inherited brain disorder with no cure. For the first time, a gene therapy has been ...
For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...
Will Forte, who played MacGruber on Saturday Night Live, and his brother-in-law Doug Modling, who has Huntington's Disease, ...
Doctors say Huntington’s disease, a fatal hereditary disorder that typically strikes in middle age, has been successfully treated for the first time as part of a small trial. Huntington’s causes ...
A novel gene therapy has been found to significantly slow the progression of Huntington’s disease, offering new hope to sufferers of the incurable disorder that destroys brain cells over time.
UniQure needs to run another trial to prove its gene therapy "actually helps people with Huntington's disease," said a senior FDA official.