Thalassemia is a common genetic condition affecting red blood cells. Children with severe forms of thalassemia often develop symptoms early in life, but effective treatment can manage the condition.

Mitapivat is the first FDA-approved oral therapy for anaemia in all forms of thalassemia Reduced transfusion dependence may improve long-term quality of life Thalassemia is an inherited blood disorder ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

Agios Pharmaceuticals said Monday that its drug called mitapivat reduced the need for blood transfusions in patients with a severe form of beta-thalassemia, an inherited blood disorder. The results ...

Detroit — The Detroit Medical Center has begun treating patients with the first gene therapy for beta-thalassemia, a rare blood disorder that causes anemia and often requires regular blood ...

Editor's note: This story was updated because an earlier version included an inaccuracy. Children's Hospital of Michigan announced Monday that it now is treating the first person in Michigan — a ...

India accounts for approximately 25 per cent of the world’s β-thalassemia cases, with an estimated 42 million carriers nationwide. Every year, between 10,000 and 15,000 children are born with ...

Beta thalassemia and sickle cell are two red blood cell disorders which both come with massive health implications and shortened lifespans, but at least for UK-based patients the former may soon be ...

The lifelong effects of rare blood disorder diagnoses in childhood are being analysed in a first-of-its-kind study led by the ...

A New York City teen was cured of a rare blood disease — just in time to spend the holidays at home with her family — thanks to a breakthrough treatment. Miriya Nurse, 16, was first diagnosed with ...

This article is authored by Dr Chandrakant Agarwal, president, Thalassemia and Sickle Cell Society.