Scientists studying axolotls, zebrafish, and mice have uncovered a shared set of genes that may one day help humans regrow ...

Regeneron Pharmaceuticals (NasdaqGS:REGN) received FDA approval for Otarmeni, the first gene therapy for genetic hearing loss ...

Six-year-old Saffie would have gone completely blind by adulthood, if not for a groundbreaking gene therapy. Her mother says ...

Trial shows promise: enGene’s gene therapy for high-risk, BCG-unresponsive bladder cancer achieved a 54% complete response rate, with low progression to advanced disease. Device gains clearance: ...

A man known as the "Toronto patient" could become the first Canadian cured of HIV. Medical experts say it's a miraculous achievement even if only a small group of people are eligible for the treatment ...

Trial results: Detalimogene achieved a 54% complete response rate in patients with high-risk, BCG-unresponsive non-muscle invasive bladder cancer. Safety profile: The therapy was generally well ...

President Donald Trump is considering firing Dr. Marty Makary after simmering frustration with his performance as FDA chief, ...

A modest wish encapsulates the dreams of his childhood: to simply live. With this heartfelt desire, Anas, an eleven-year-old ...

New breast cancer pill eliminates tumor proteins and improves treatment response in patients by making the estrogen receptor ...

Recently, the novel oral BET inhibitor NHWD-870 HCI, independently developed by Zhejiang Wenda Pharmaceutical Technology Co., Ltd., officially received ...

Rznomics’ investigational trans-splicing ribozyme-based RNA therapy for hepatocellular carcinoma. The designation is ...