News

EconoTimes52m
Roche Halts Elevidys Dosing in Some Duchenne Patients After Fatalities
Roche (SIX:ROG) shares dropped 2% on Monday after the company paused dosing of its gene therapy Elevidys in non-ambulatory ...
Questions over cost of muscular dystrophy drug in Belfast Trust
The drug, Givinostat, has been approved as safe for use but Belfast Health Trust, NI's specialist centre for the condition, ...
Sarepta Provides Safety Update for ELEVIDYS and Initiates Steps to Strengthen Safety in Non-Ambulatory Individuals with Duchenne
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today provided a safety ...
Hosted on MSN13d
Cardiac Complications of Duchenne Muscular Dystrophy
Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies ...
The American Journal of Managed Care3d
RGX-202 Gene Therapy Improves DMD Trajectory, Biomarkers
Participants with Duchenne muscular dystrophy (DMD) who received RGX-202 demonstrated functional improvement and better ...
RTÉ Ireland4d
Families call for approval of new 'game changer' Muscular Dystrophy drug
Parents of children with an incurable muscle-wasting condition have called on the Minister for Health to accelerate the ...
New hope for Deal family of nine-year-old boy with Duchenne muscular dystrophy
The parents of a nine-year-old boy battling a devastating muscle-wasting condition say new research could offer them more ...
Managed Healthcare Executive12d
Encouraging Results from Phase 1 Trials, Says Satellos Chief Scientific Officer. Now It's On to Phase 2
Satellos Bioscience Chief Scientific Officer discusses early-stage trials of the company's Duchenne muscular dystrophy drug, ...
Capricor Therapeutics Announces Key Regulatory Updates for its Duchenne Muscular Dystrophy Program
U.S. FDA successfully completed Pre-License Inspection; Company expects facility will meet all requirements to support ...
Medical Marketing & Media6d
How the Muscular Dystrophy Association celebrated 75 years of research
The campaign to commemorate the work of the Muscular Dystrophy Association was created in partnership with agency Yes&.